James Wilson, director of the Institute for Human Gene Therapy at the University of Pennsylvania Medical Center, explained that because gene therapy vectors spread beyond the site of distribution ...

The supply of most gene therapies under development still relies on processes created in the 1970s, requiring huge reactors to produce tiny amounts of product, Vigneault explained. “We’ve re ...

Gene therapy partially restores visual processing ... the burden of treatment remain barriers to access and utilization, explained Kevin Niehoff, PharmD, BCMAS, of IPD Analytics.

Common measurements for modified adeno-associated viruses (AAVs), a gene therapy delivery method, showed substantial ...

Patrick Hsu, co-founder of the Arc Institute, explained that this allows for ... these disease-causing genetic sequences entirely.” Gene Therapy Allows a Deaf Child to Hear For the First Time ...

This trial marks a new frontier in gene therapy – the process of treating or curing medical conditions by changing a person’s genes. What makes it special is the fact the therapy targets RNA ...

VP & global program head of some of Novartis’ gene therapy projects, explained in an interview with Fierce Pharma. The goal is to get Zolgensma into a larger, older patient population.

Researchers at Washington University School of Medicine in St. Louis have described the neurodegeneration that occurs in the ...